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Table 2 Identified patient access schemes in Australia

From: Patient access schemes in Asia-pacific markets: current experience and future potential

Technology

Indication

Company

Payer

Type

Source

Cancer (n = 29)

Dasatinib

CML

Bristol-Myers Squibb Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Nilotinib

CML

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Imatinib

GIST, adjuvant

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Imatinib

GIST, metastatic

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Lapatinib

Late stage metastatic breast cancer

GlaxoSmithKline Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Imatinib

Rare cancers (eg dermatofibrosarcoma protuberans, chronic eosinophilic leukemia)

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Pazopanib

RCC

GlaxoSmithKline Australia Pty Ltd

PBS

Financially-based; Outcome-based

Public Summary Document [18]

Bevacizumab

Metastatic colorectal cancerr

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

Public Summary Document [18]

Sorafenib

Advanced hepatocellular carcinoma

Bayer Australia Ltd

PBS

Financially-based; Outcome-based

Public Summary Document [18]

PET

Staging of newly diagnosed NSCLC, esophageal cancer, cancer of gastro-esophageal junction, head and neck cancer, suspected residual/metastatic/recurrent colorectal cancer, melanoma, head and neck cancer, ovarian cancer

Not specified

MBS

Evidence generation

Stafinski et al. 2010 [15]

Exemestane

Oestrogen-receptor positive advanced breast cancer in post-menopausal women

Pfizer Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Imiquimod

Superficial basal cell carcinoma

3 M Pharmaceuticals Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Letrozole

Advanced breast cancer in postmenopausal women

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Docetaxel

SCCHN

Sanofi-Aventis Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Sunitinib

RCC

Pfizer Australia Pty Ltd

PBS

Financially-based

PBS Schedule [16], Public Summary Document [18]

Cetuximab

K-RAS wild mCRC

Merck Serono Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Vemurafenib

Untreated unresectable stage IIIC or stage IV melanoma

Roche Products Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Imatinib

ALL

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Dasatinib

ALL

Bristol-Myers Squibb Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Azacitidine

CML

Celgene Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Azacitidine

AML

Celgene Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Azacitidine

Myelodysplastic syndrome

Celgene Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Imatinib

CML

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Trastuzumab

HER2+ early breast cancer

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Sunitinib

GIST

Pfizer Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Lenalidomide

Myelodysplastic syndrome

Celgene Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Lenalidomide

Multiple myeloma

Celgene Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Bortezomib

Multiple myeloma

Janssen-Cilag Pty Ltd

PBS

Financially-based, Outcome-based

PBS Schedule [16], PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Erlotinib

Non-small cell lung cancer

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Inflammatory Conditions (n = 28)

Adalimumab

Ankylosing spondylitis

AbbVie Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Etanercept

Ankylosing spondylitis

Pfizer Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Golimumab

Ankylosing spondylitis

Janssen-Cilag Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Infliximab

Ankylosing spondylitis

Janssen-Cilag Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Adalimumab

Crohn’s disease

AbbVie Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Infliximab

Complex refractory fistulising Crohn’s disease

Janssen-Cilag Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Adalimumab

Juvenile arthritis

AbbVie Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Etanercept

Juvenile arthritis

Pfizer Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Adalimumab

Psoriatic arthritis

AbbVie Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Golimumab

Psoriatic arthritis

Janssen-Cilag Pty Ltd(

PBS

Outcome-based

Medicare Australia [14]

Infliximab

Psoriatic arthritis

Janssen-Cilag Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Pimecrolimus

Atopic dermatitis who are over 18 years of age

Novartis Pharmaceuticals Australia

PBS

Financially-based

Public Summary Document [18]

Infliximab

Crohn’s disease

Janssen-Cilag Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Adalimumab

Complex refractory fistulising Crohn’s disease

AbbVie Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Tocilizumab

Juvenile arthritis

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Abatacept

RA

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Infliximab

RA

Janssen-Cilag Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Lu et al. 2007 [33], Pugatch et al. 2010 [21], Medicare Australia [14]

Rituximab

RA

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Lu et al. 2007 [33], Pugatch et al. 2010 [21], Medicare Australia [14]

Tocilizumab

RA

Roche Products Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Certolizumab Pegol

RA

UCB Australia Proprietary Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Adalimumab

RA

AbbVie Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Lu et al. 2007 [33], Pugatch et al. 2010 [21], Medicare Australia [14]

Golimumab

RA

Janssen-Cilag Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Etanercept

RA

Pfizer Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Lu et al. 2007 [33], Pugatch et al. 2010 [21], Medicare Australia [14]

Adalimumab

Severe chronic plaque psoriasis

AbbVie Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Lu et al. 2007 [33], Pugatch et al. 2010 [21], Medicare Australia [14]

Etanercept

Severe chronic plaque psoriasis

Pfizer Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Infliximab

Severe chronic plaque psoriasis

Janssen-Cilag Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Ustekinumab

Severe chronic plaque psoriasis

Janssen-Cilag Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Etanercept

Severe chronic plaque psoriasis under 18

Pfizer Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Infectious Diseases (n = 7)

Abacavir

HIV infection

ViiV Healthcare Pty Ltd

PBS

Financially-based

Robertson et al. 2009 [19], Adamski et al. 2010 [20]

Tipranavir

HIV infection

Boehringer Ingelheim Pty Ltd

PBS

Financially-based

PBS Schedule [16], Public Summary Document [18]

Entecavir

Chronic hepatitis B in adults 16 years and older with evidence of active liver inflammation

Bristol-Myers Squibb Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Boceprevir

Chronic genotype 1 hepatitis C infection

Merck Sharp & Dohme (Australia) Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Telaprevir

Chronic genotype 1 hepatitis C

Janssen-Cilag Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Posaconazole

Invasive fungal infections, not responsive to or intolerant of, alternative therapy

Schering-Plough Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Posaconazole

Prophylaxis of invasive fungal infections among high risk patients

Schering-Plough Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Pulmonary Hypertension (n = 7)

Sildenafil

PPH or PAH

Pfizer Australia Pty Ltd

PBS

Outcome-based

PBS Schedule [16], Medicare Australia [14]

Tadalafil

PPH or PAH

Eli Lilly Australia Pty Ltd

PBS

Outcome-based

PBS Schedule [16], Medicare Australia [14]

Treprostinil Sodium

PPH or PAH

Orphan Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Ambrisentan

PPH or PAH

GlaxoSmithKline Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Bosentan

PPH or PAH

Actelion Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Epoprostenol

PPH or PAH

GlaxoSmithKline Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Iloprost trometamol

PPH or PAH

Bayer Australia Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Other (n = 27)

Modafinil

Narcolepsy

bioCSL (Australia) Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Verteporfin

Age-related macular degeneration

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Outcome-based

Medicare Australia [14]

Deep brain stimulation

Patients with Parkinson's disease no longer responsive to drug therapy

Not specified

MBS

Evidence generation

Stafinski et al. 2010 [15]

EVAR

Abdominal aortic aneurysm

Not specified

MBS

Evidence generation

Stafinski et al. 2010 [15]

Dabigatran

Prevention of stroke or systemic embolism in patients with non-valvular atrial fibrillation

Boehringer Ingelheim Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Atomoxetine Hydrochloride

ADHD diagnosed between the ages of 6 and 18 years

Eli Lilly Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Fingolimod

RRMS

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

Public Summary Document [18]

Cinacalcet Hydrochloride

End stage renal disease receiving dialysis who have uncontrolled secondary hyperparathyroidism

Amgen Australia Pty Ltd

PBS

Financially-based

PBS Schedule [16], Public Summary Document [18]

Clostridium botulinum type A toxin-haemagglutinin complex

Severe spasticity of the upper limb in adults following a stroke, as an adjunct to physical therapy

Ipsen Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Fentanyl citrate

Fentanyl lozenges for the treatment of breakthrough pain

Orphan Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Natalizumab

RRMS

Biogen Idec Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Paliperidone

Schizophrenia

Janssen-Cilag Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Botulinum toxin type a purified neurotoxin complex

Moderate to severe spasticity of the upper limb in adults following a stroke as an adjunct to physical therapy

Allergan Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Tenofovir Disoproxil Fumarate

Treatment of chronic hepatitis B

Gilead Sciences Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Pramipexole hydrochloride

Idiopathic Parkinson disease

Boehringer Ingelheim Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Tobramycin

Pseudomonas aeruginosa respiratory infection in a patient with Cystic Fibrosis

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Ticagrelor

ACS, MI, or unstable angina

AstraZeneca Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Pregabalin

Neuropathic pain

Pfizer Australia Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Rivaroxaban

Acute symptomatic DVT

Bayer Australia Ltd

PBS

Financially-based

Public Summary Document [18]

Aztreonam

Pseudomonas aeruginosa infection in patients with cystic fibrosis

Gilead Sciences Pty Ltd

PBS

Financially-based

Public Summary Document [18]

Crinone (progesterone gel)

Supplement progesterone in women who have luteal phase defect

Merck Serono

PBS

Financially-based

Robertson et al. 2009 [19], Adamski et al. 2010 [20]

Deferasirox (Exjade)

Chronic iron overload in patients with disorders of erythropoiesis

Novartis

PBS

Financially-based

Robertson et al. 2009 [19], Adamski et al. 2010 [20]

Omalizumab

Uncontrolled severe allergic asthma

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Aflibercept

Age-related macular degeneration

Bayer Australia Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

Ranibizumab

Age-related macular degeneration

Novartis Pharmaceuticals Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], PBPA Relativity Sheets [17], Public Summary Document [18], Medicare Australia [14]

Eltrombopag

Severe chronic immune idiopathic thrombocytopenic purpura

GlaxoSmithKline Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBPA Relativity Sheets [17], Medicare Australia [14]

Romiplostim

Severe chronic immune idiopathic thrombocytopenic purpura

Amgen Australia Pty Ltd

PBS

Financially-based; Outcome-based

PBS Schedule [16], Medicare Australia [14]

  1. ACS = Acute Coronary Syndromes; ALL = Acute Lymphoblastic Leukemia; AML = Acute Myeloid Leukemia; CML = Chronic Myeloid Leukemia; DVT = Deep Vein Thrombosis; EVAR = endovascular aneurysm repair; GIST = Gastrointestinal Stromal Tumor; MBS = Medicare Benefits Schedule; mCRC = Metastatic Colorectal Cancer; MI = Myocardial Infarction; PAH = Pulmonary Arterial Hypertension; PBS = Pharmaceutical Benefits Scheme; PPH = Primary Pulmonary Hypertension; RA = Rheumatoid Arthritis; RCC = Renal Cell Carcinoma; RRMS = Relapsing-Remitting Multiple Sclerosis; SCCHN = Squamous Cell Carcinoma of the Head and Neck.